Sarepta, with new data, plans final push for limb-girdle gene therapy

Sarepta, with new data, plans final push for limb-girdle gene therapy

Source: 
BioPharma Dive
snippet: 

Sarepta Therapeutics on Monday added to a small, but growing, body of evidence that one of its experimental gene therapies might help treat a potentially deadly genetic disease called limb-girdle muscular dystrophy.