Genentech Announces New Data for Risdiplam in Spinal Muscular Atrophy in Infants

Genentech Announces New Data for Risdiplam in Spinal Muscular Atrophy in Infants

Source: 
CP Wire
snippet: 
  • During 8 month visit 57% of infants showed improvement during time when most with Type 1 SMA show no improvement or decline
  • Risdiplam is delivered orally
  • Risdiplam is being co-developed with PTC Therapeutics