Alnylam Submits NDA in Japan for Onpattro for Hereditary ATTR Amyloidosis

Alnylam Submits NDA in Japan for Onpattro for Hereditary ATTR Amyloidosis

Source: 
CP Wire
snippet: 
  • Patisiran is approved in the US for hATTR
  • It has orphan drug status in the US and Japan
  • Patisiran is elegible for priority review in Japan