Alnylam phase 3 links lumasiran to 'clinically significant' improvement in infants

Alnylam phase 3 links lumasiran to 'clinically significant' improvement in infants

Source: 
Fierce Biotech
snippet: 

A phase 3 trial has linked Alnylam’s lumasiran to a “clinically significant” decline in a substance that drives negative outcomes in children with a rare kidney disease. The top-line readout comes months before the FDA is due to rule on whether to approve the RNAi therapeutic in older patients.