Alnylam makes case for lumasiran in infants ahead of FDA ruling

Alnylam makes case for lumasiran in infants ahead of FDA ruling

Source: 
Fierce Biotech
snippet: 

Alnylam has shared data from a phase 3 trial of its near-approval kidney disease drug lumasiran in children as young as three months. The RNAi therapy drove a 72% reduction in urinary oxalate from baseline, boosting Alnylam’s hopes of using the drug in a broad patient population.