spinal muscular atrophy

Roche, PTC post latest SMA data from their attempt to rival Spinraza, Zolgensma
Roche, PTC post latest SMA data from their attempt to rival Spinraza, Zolgensma
Fierce Biotech
Roche
PTC Therapeutics
spinal muscular atrophy
risdiplam
Novartis
Zolgensma
Biogen
Spinraza
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New Zolgensma data suggest comparable efficacy to Spinraza — analysts
New Zolgensma data suggest comparable efficacy to Spinraza — analysts
Endpoints
Novartis
FDA
spinal muscular atrophy
Zolgensma
AveXis
Biogen
Spinraza
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Novartis makes final Zolgensma pitch before FDA decision
Novartis makes final Zolgensma pitch before FDA decision
BioPharma Dive
Novartis
gene therapy
Zolgensma
FDA
spinal muscular atrophy
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SMA Moment: Will Gene Therapy Shift Treatment, Costs of Muscle Disease?
SMA Moment: Will Gene Therapy Shift Treatment, Costs of Muscle Disease?
Xconomy
gene therapy
SMA
spinal muscular atrophy
Novartis
Zolgensma
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Novartis mulling $1.5 mln-$5 mln price range for SMA gene therapy
Novartis mulling $1.5 mln-$5 mln price range for SMA gene therapy
Yahoo/Reuters
Novartis
Zolgensma
gene therapy
drug pricing
spinal muscular atrophy
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Ionis slides after AveXis reports SMA data for Zolgensma
Ionis slides after AveXis reports SMA data for Zolgensma
BioCentury
Ionis Pharmaceuticals
AveXis
Zolgensma
lcinical trials
spinal muscular atrophy
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With FDA decision near, Novartis bolsters SMA gene therapy case
With FDA decision near, Novartis bolsters SMA gene therapy case
Biopharma Dive
Novartis
FDA
Zolgensma
spinal muscular atrophy
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Novartis' SMA gene therapy would not be cost-effective if priced over $1.5M: ICER
Novartis' SMA gene therapy would not be cost-effective if priced over $1.5M: ICER
Fierce Pharma
Novartis
ICER
drug pricing
Zolgensma
gene therapy
spinal muscular atrophy
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ICER's life year calculation gives Novartis wider pricing ballpark for SMA therapy
ICER's life year calculation gives Novartis wider pricing ballpark for SMA therapy
BioCentury
Novartis
Zolgensma
AVXS-101
spinal muscular atrophy
ICER
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Novartis: Alternative payments will ‘reset the paradigm’ for covering gene, cell therapies
Novartis: Alternative payments will ‘reset the paradigm’ for covering gene, cell therapies
Fierce Pharma
Novartis
ICER
spinal muscular atrophy
alternative payments
drug pricing
gene therapy
Zolgensma
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ICER says gene therapy may be more cost effective for spinal muscular atrophy
ICER says gene therapy may be more cost effective for spinal muscular atrophy
Yahoo/Reuters
Biogen
Spinraza
Novartis
spinal muscular atrophy
ICER
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US benefits manager baulks after Novartis values gene therapy at $4-5 mln
US benefits manager baulks after Novartis values gene therapy at $4-5 mln
Yahoo/Reuters
Novartis
Express Scripts
SMA
spinal muscular atrophy
drug pricing
AVXS-101
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Sticker shock: Novartis says its top drug prospect is worth $4M-$5M for a once-and-done use
Sticker shock: Novartis says its top drug prospect is worth $4M-$5M for a once-and-done use
Endpoints
Novartis
drug pricing
AVXS-101
spinal muscular atrophy
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Biogen's new Spinraza data for earlier use 'pretty amazing,' analyst says
Biogen's new Spinraza data for earlier use 'pretty amazing,' analyst says
Fierce Pharma
Biogen
Spinraza
spinal muscular atrophy
SMA
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Genentech Announces New Data for Risdiplam in Spinal Muscular Atrophy in Infants
Genentech Announces New Data for Risdiplam in Spinal Muscular Atrophy in Infants
CP Wire
Genentech/Roche
risdiplam
spinal muscular atrophy
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Genentech Announces New Data for Risdiplam in Spinal Muscular Atrophy in Infants
Genentech/Roche
risdiplam
spinal muscular atrophy
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[video+transcript]Gene Therapy Could Be a Boon for This Biotech
[video+transcript]Gene Therapy Could Be a Boon for This Biotech
Motley Fool
gene therapy
Rengexbio
spinal muscular atrophy
wet age-related macular degeneration
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Biogen's Spinraza gets an early no-go from NICE
Biogen's Spinraza gets an early no-go from NICE
Biopharma Dive
Biogen
UK
NICE
Spinraza
SMA
spinal muscular atrophy
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Why PTC Therapeutics Dropped 30.6% Today After Jumping 27.5% Yesterday
Why PTC Therapeutics Dropped 30.6% Today After Jumping 27.5% Yesterday
Motley Fool
PTC Therapeutics
risdiplam
Biogen
Ionis Pharmaceuticals
spinal muscular atrophy
Sarepta Therapeutics
Translarna
Emflaza
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After a crushing PhIII failure, Cytokinetics says its next-gen muscle drug is lining up well in PhII — but big challenges loom
After a crushing PhIII failure, Cytokinetics says its next-gen muscle drug is lining up well in PhII — but big challenges loom
Endpoints
Cytokinetics
clinical trials
reldesemtiv
Tirasemtiv
spinal muscular atrophy
Astellas
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