spinal muscular atrophy

US benefits manager baulks after Novartis values gene therapy at $4-5 mln
US benefits manager baulks after Novartis values gene therapy at $4-5 mln
Yahoo/Reuters
Novartis
Express Scripts
SMA
spinal muscular atrophy
drug pricing
AVXS-101
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Sticker shock: Novartis says its top drug prospect is worth $4M-$5M for a once-and-done use
Sticker shock: Novartis says its top drug prospect is worth $4M-$5M for a once-and-done use
Endpoints
Novartis
drug pricing
AVXS-101
spinal muscular atrophy
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Biogen's new Spinraza data for earlier use 'pretty amazing,' analyst says
Biogen's new Spinraza data for earlier use 'pretty amazing,' analyst says
Fierce Pharma
Biogen
Spinraza
spinal muscular atrophy
SMA
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Genentech Announces New Data for Risdiplam in Spinal Muscular Atrophy in Infants
Genentech Announces New Data for Risdiplam in Spinal Muscular Atrophy in Infants
CP Wire
Genentech/Roche
risdiplam
spinal muscular atrophy
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Genentech Announces New Data for Risdiplam in Spinal Muscular Atrophy in Infants
Genentech/Roche
risdiplam
spinal muscular atrophy
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[video+transcript]Gene Therapy Could Be a Boon for This Biotech
[video+transcript]Gene Therapy Could Be a Boon for This Biotech
Motley Fool
gene therapy
Rengexbio
spinal muscular atrophy
wet age-related macular degeneration
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Biogen's Spinraza gets an early no-go from NICE
Biogen's Spinraza gets an early no-go from NICE
Biopharma Dive
Biogen
UK
NICE
Spinraza
SMA
spinal muscular atrophy
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Why PTC Therapeutics Dropped 30.6% Today After Jumping 27.5% Yesterday
Why PTC Therapeutics Dropped 30.6% Today After Jumping 27.5% Yesterday
Motley Fool
PTC Therapeutics
risdiplam
Biogen
Ionis Pharmaceuticals
spinal muscular atrophy
Sarepta Therapeutics
Translarna
Emflaza
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After a crushing PhIII failure, Cytokinetics says its next-gen muscle drug is lining up well in PhII — but big challenges loom
After a crushing PhIII failure, Cytokinetics says its next-gen muscle drug is lining up well in PhII — but big challenges loom
Endpoints
Cytokinetics
clinical trials
reldesemtiv
Tirasemtiv
spinal muscular atrophy
Astellas
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Roche scraps €120M SMA drug after hitting ‘many difficulties’
Roche scraps €120M SMA drug after hitting ‘many difficulties’
Fierce Biotech
Roche
SMA
spinal muscular atrophy
Olesoxime
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Biogen’s Spinraza Sales Slow as AveXis and Novartis Pursue SMA Gene Therapy
Biogen’s Spinraza Sales Slow as AveXis and Novartis Pursue SMA Gene Therapy
Xtalks
Biogen
earnings
Spinraza
spinal muscular atrophy
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First Patient Dosed in Avexis' Phase 3 Trial of AVXS-101 in Pre-Symptomatic Spinal Muscular Atrophy
First Patient Dosed in Avexis' Phase 3 Trial of AVXS-101 in Pre-Symptomatic Spinal Muscular Atrophy
CP Wire
AveXis
Novartis
M&A
clinical trials
AVXS-101
gene therapy
spinal muscular atrophy
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Novartis buying AveXis for $8.7 billion to strengthen gene therapy capabilities
Novartis buying AveXis for $8.7 billion to strengthen gene therapy capabilities
Stat
Novartis
M&A
AveXis
gene therapy
AVXS-101
SMA
spinal muscular atrophy
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Biogen Unlikely To See Spinraza Rival In 2018 As AveXis Delayed
Biogen Unlikely To See Spinraza Rival In 2018 As AveXis Delayed
Investors Business Daily
Biogen
Spinraza
AveXis
AVXS-101
spinal muscular atrophy
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NEJM publishes Phase III results for Biogen/Ionis’ Spinraza
NEJM publishes Phase III results for Biogen/Ionis’ Spinraza
GoinPharma
Biogen
Ionis Pharmaceuticals
Spinraza
clinical trials
spinal muscular atrophy
SMA
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US Spinraza sales cause concern among Biogen investors
US Spinraza sales cause concern among Biogen investors
Biopharma Dive
Biogen
Spinraza
spinal muscular atrophy
investors
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Spinraza launch set for blockbuster trajectory
Spinraza launch set for blockbuster trajectory
BioPharma Dive
Spinraza
Biogen
SMA
spinal muscular atrophy
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For Biogen's Spinraza launch, things are looking up on the coverage front: analyst
For Biogen's Spinraza launch, things are looking up on the coverage front: analyst
Fierce Pharma
Biogen
Spinraza
drug launches
spinal muscular atrophy
SMA
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PTC and Roche report solid data for Spinraza rival
PTC and Roche report solid data for Spinraza rival
BioPharma Dive
PTC Therapeutics
Roche
Spinraza
Biogen
RG7916
SMA
spinal muscular atrophy
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Biogen’s Spinraza Witnessed Robust Patient Demand in 1Q17
Biogen’s Spinraza Witnessed Robust Patient Demand in 1Q17
Market Realist
Biogen
Spinraza
patients
SMA
spinal muscular atrophy
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