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» molybdenum cofactor deficiency type A
molybdenum cofactor deficiency type A
BridgeBio spins gold out of an Alexion castoff, scoring an FDA approval in rare metabolism disorder
Endpoints
Mon, 03/1/21 - 10:36 am
BridgeBio
fosdenopterin
Nulibry
ALXN1101
molybdenum cofactor deficiency type A
FDA
Alexion