GTX-102

Ultragenyx says Angelman therapy is working, but safety questions remain
BioPharma Dive
Tue, 04/16/24 - 07:49 am
Ultragenyx
Angelman Syndrome
GTX-102
Acasti, seeking to expand use of old steroid, posts clinical data on oral spray in rare disease
Fierce Pharma
Tue, 01/3/23 - 10:40 am
Acasti Pharma
betamethasone
Rare Diseases
GTX-102
ataxia telangiectasia
Ultragenyx granted go-ahead to up doses for Angelman antisense therapy that stalled after safety issues
Fierce Biotech
Wed, 01/5/22 - 10:32 pm
Ultragenyx
GeneTx Biotherapeutics
Angelman Syndrome
clinical trials
antisense
GTX-102
Ultragenyx pauses antisense trial after patients lose ability to walk
Fierce Biotech
Tue, 10/27/20 - 10:40 am
Ultragenyx
clinical trials
GTX-102
antisense