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beta thalassemia
With LentiGlobin cleared by FDA, bluebird lifts EU marketing hold on gene therapy using the same delivery mechanism
Endpoints
Fri, 07/9/21 - 09:54 am
Bluebird Bio
LentiGlobin
sickle cell disease
Zynteglo
Europe
beta thalassemia
CRISPR and Vertex Release Additional Data for Blood Disease Treatment
Motley Fool
Wed, 11/4/20 - 10:50 pm
CRISPR Therapeutics
CRISPR
Vertex Pharmaceuticals
CTX001
beta thalassemia
sickle cell disease
EdiGene raises $67M to take gene-editing therapies into humans
Fierce Biotech
Tue, 10/13/20 - 11:09 am
EdiGene
gene editing
CAR-T
beta thalassemia
ET-01
ET-02
CRISPR and Vertex show durability of gene-editing therapy, hoping for one and done treatment
Fierce Biotech
Mon, 06/15/20 - 10:35 am
Vertex Pharmaceuticals
CRISPR Therapeutics
CTX001
gene editing
sickle cell disease
beta thalassemia
Magenta, Beam partner to explore use of antibody-based conditioning drug for gene therapies
MedCity News
Mon, 06/15/20 - 10:25 am
Magenta Therapeutics
Beam Therapeutics
MGTA-117
gene therapy
sickle cell disease
beta thalassemia
New CRISPR, gene therapy results strengthen potential for treatment of blood diseases
BioPharma Dive
Fri, 06/12/20 - 11:11 am
CRISPR
gene therapy
beta thalassemia
sickle cell disease
CRISPR Therapeutics
Vertex
Bluebird Bio
EHA
FDA Mishaps Have Investors Asking “What’s Going On With bluebird bio?”
Motley Fool
Sun, 05/24/20 - 10:19 pm
Bluebird Bio
beta thalassemia
LentiGlobin
FDA
pandemic
clinical trials
Why So Many Biotechs Are Scrambling to Develop a Drug for the Same Rare Disease
Motley Fool
Sun, 02/23/20 - 06:17 pm
beta thalassemia
rare disease
drug development
Acceleron
Bristol-Myers Squibb
Bluebird Bio
Sangamo Therapeutics
Vertex Pharmaceuticals
Editas Medicine
Syros Pharmaceuticals
Blood disorder startup files for $86M IPO
Bizjournals
Wed, 02/19/20 - 09:52 am
IPOs
Imara
sickle cell disease
beta thalassemia
Biotech Stock Pops On Promising First In-Human CRISPR Gene-Editing Drug
Investors Business Daily
Wed, 11/20/19 - 09:53 am
CRISPR Therapeutics
gene editing
CRISPR
beta thalassemia
sickle cell disease
FDA Approves Celgene and Acceleron's Treatment for Rare Blood Disease
BioSpace
Sat, 11/9/19 - 12:13 pm
Celgene
Acceleron
Reblozyl
anemia
beta thalassemia
Genetic Disease Focused Fulcrum Therapeutics Files for $86 Million IPO
CP Wire
Mon, 06/24/19 - 09:32 am
Fulcrum Therapeutics
IPOs
FSHD
sickle cell disease
beta thalassemia
Genetic Disease Focused Fulcrum Therapeutics Files for $86 Million IPO
Mon, 06/24/19 - 09:29 am
Fulcrum Therapeutics
IPOs
FSHD
sickle cell disease
beta thalassemia
What Bluebird Bio Gets Wrong In Pricing For Its $1.8 Million Drug
Forbes
Wed, 06/19/19 - 09:55 am
Bluebird Bio
gene therapy
drug pricing
Zynteglo
beta thalassemia
bluebird offers installment payments for Zynteglo gene therapy
Pharmaforum
Mon, 06/17/19 - 12:25 pm
Bluebird Bio
outcome-based pricing
drug pricing
gene therapy
Zynteglo
beta thalassemia
Is $1.8 Million for bluebird bio's New Gene Therapy Ridiculous?
Motley Fool
Sat, 06/15/19 - 05:49 pm
Bluebird Bio
Zynteglo
drug pricing
beta thalassemia
Bluebird sets $1.8M price tag for blood-disease gene therapy
Biopharma Dive
Fri, 06/14/19 - 12:08 pm
drug pricing
Bluebird Bio
Zynteglo
Europe
beta thalassemia
Patients, payers await pricing plans for bluebird's first approved gene therapy
BioCentury
Tue, 06/4/19 - 11:04 am
Bluebird Bio
gene therapy
Zynteglo
drug pricing
beta thalassemia
In a much-needed positive for BMS, Celgene gains FDA review for blockbuster hopeful
Fierce Biotech
Tue, 06/4/19 - 11:02 am
Celgene
Bristol-Myers Squibb
Acceleron
luspatercept
MDS
beta thalassemia
Bluebird Bio’s Gene Therapy for Blood Disease Wins European Approval
Xconomy
Mon, 06/3/19 - 07:50 pm
Bluebird Bio
gene therapy
Europe
Zynteglo
EMA
beta thalassemia
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